California Observer

June 20, 2026

UC Riverside Study Tests Gene Therapy for Fragile X Syndrome

UC Riverside Study Tests Gene Therapy for Fragile X Syndrome

Fragile X gene therapy research at the University of California, Riverside has produced new findings after scientists reported that an experimental treatment restored normal brain activity and reversed key deficits in a mouse model of Fragile X syndrome. The study involved researchers from UC Riverside who investigated whether targeted genetic intervention could address neurological abnormalities […]

UC Riverside Study Tests Gene Therapy for Fragile X Syndrome Read More »